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Small Biotechs
Five Small Biotechs to Watch: March 2025
David Alvaro, Ph.D.
Pharma's Almanac
PAO-02-25-CL-21
Feb 28, 2025
Radioconjugates
Rising Interest in Radioconjugate Therapies
Cynthia A. Challener, Ph.D.
Pharma's Almanac
PAO-02-25-CL-20
Feb 25, 2025
Approval
Anixa Biosciences Announces Approval of Protocol Amendment for Ovarian Cancer CAR-T Clinical Trial
Anixa Biosciences
PR-02-25-NI-16
Feb 19, 2025
Gene Therapy
Genprex Provides Update on Diabetes Gene Therapy Program
Genprex
PR-02-25-NI-15
Feb 19, 2025
xRNA
Revolutionizing xRNA Production: The Economic Case for Continuous Manufacturing
Aaron B. Cowley, Ph.D.
ReciBioPharm
PAO-02-25-CL-11
Feb 13, 2025
Clinical Trials
EXUMA Biotech Announces Phase 1 Results for its Autologous HER2 Directed CAR-T Product at ASCO GI 2025
EXUMA Biotechnology
PR-01-25-NI-26
Feb 11, 2025
Clinical Trials
CARsgen's First Enrolled Subject in the THANK-u Plus™ Platform-Based Allogeneic CAR-T Trial Achieves sCR at Week 4
Carsgen Therapeutics
PR-02-25-NI-09
Feb 11, 2025
RNA
Enabling Cost-Effective, Rapid Access to RNA Vaccines and Therapeutics with Enzymatically Generated z- dbDNA
Lisa Caproni
Touchlight
PAO-01-25-CL-08
Feb 10, 2025
Cell Therapy
From Research to Clinical Trials to Commercialization: Advancing CGT with Frozen Cellular Starting Materials
Dominic Mancini
OrganaBio
PAO-01-25-CL-13
Jan 28, 2025
Advanced Therapies
Ensuring Nuclease Free Process Consumables for Biopharma Applications
Richard Fry
Sanisure
PAO-01-25-CL-05
Jan 22, 2025
Protein Portfolio
Bio-Techne Expands R&D Systems AI-Engineered Designer Protein Portfolio to Advance Cell Therapy and Regenerative Medicine
Bio-Techne Corporation
PR-01-25-NI-05
Jan 10, 2025
Sustainability
Synthetic DNA Delivers a Sustainable Future for Genetic Medicines
Touchlight
PAO-01-25-CL-04
Jan 07, 2025
RNA
Screening T7 Polymerases to Optimize xRNA Yield and Quality
Jing Zhu, Ph.D.
ReciBioPharm
PAO-01-25-CL-02
Jan 07, 2025
Announcement
Nona Biosciences Announces Update on Its Collaborator DualityBio's Antibody-Drug Conjugate (ADC) Collaboration with BeiGene
Nona Biosciences
PR-01-25-NI-02
Jan 03, 2025
Nonviral Delivery
Rewriting the Rules of Gene Therapy with Nonviral DNA Delivery using dbDNA
Lisa Caproni
Touchlight
PAO-12-24-CL-4
Dec 16, 2024
Clinical Trials
Beacon Therapeutics Announces Positive 3-Month Data from Phase 2 DAWN Trial in Patients
Beacon Therapeutics
PR-12-24-NI-131
Dec 06, 2024
AAV Quality
Improving AAV Vector Quality with In-Process Monitoring of Capsid Formation
Nathan Sweeney, Ph.D.; Hena Divanovic, M.Sc.
Rentschler Biopharma SE
PAO-11-24-CL-06
Dec 02, 2024
CASGEVY
Orsini Now Distributing CASGEVY® (exagamglogene autotemcel), a Gene-Editing Therapy
Orsini Healthcare
PR-11-24-NI-103
Nov 15, 2024
Gene Therapy
FDA Approves First Gene Therapy for Treatment of Aromatic L-amino Acid Decarboxylase Deficiency
U.S. Food & Drug Administration
PR-11-24-NI-100
Nov 15, 2024
RNA
Lexogen launches Streamlined, Large-scale RNA-Seq Service for Blood Samples
Lexogen
PR-11-24-NI-99
Nov 15, 2024